Endocrinology Trials

  • 30/06/2021

    ORION-3

    An open label active comparator extension trial to assess the effect of long term dosing of inclisiran and evolocumab given as subcutaneous injections in subjects with high cardiovascular risk and elevated LDL-C (ORION-3)

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  • 30/09/2019

    GalNET

    European registry and network for Galactosemias (GalNET)

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  • 31/10/2019

    Dietary management clinical status and outcome of patients with Citrin deficiency in the UK

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  • 30/04/2022

    A Comparison of the Natural History of Patients with and without Familial Chylomicronaemia Syndrome (FCS).

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  • 31/01/2020

    Blood phenylalanine control of patients with Phenylketonuria in the UK

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  • 31/01/2021

    A Phase 2 Randomized Placebo-Controlled Study of Safety and Efficacy Following Repeat-Dose Administration of Evinacumab (anti-ANGPTL3) in Patients with Severe Hypertriglyceridemia (sHTG) at Risk for Acute Pancreatitis

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  • 29/06/2018

    Development of health-related quality of life scales for patients and parents affected by Niemann-Pick Disease Type C

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  • 01/05/2025

    MARS

    MORQUIO A REGISTRY STUDY(MARS)

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  • 18/11/2015

    PKU Lophlex New Format – acceptability and tolerance (market research)

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  • 31/12/2019

    An Open-Label Rollover Study of PBI-4050 in Subjects with Alström Syndrome

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